Determining Appropriate Clinical Endpoints for CNS Gene Therapies to Treat Neurodegenerative Disorders
Time: 9:00 am
day: Day Two Whole
Details:
- Successfully detecting significant changes in a slow-progressing disease within the timeframe of a clinical trial
- Utilizing a dual endpoint strategy to combine surrogate and clinical endpoints to gain a comprehensive picture of the gene therapies impact in the CNS
- Discussing novel techniques to analyze patients and define specific patient subgroups, disease status
