About Event

7th Gene Therapy for CNS Summit – What’s it About?

The 7th Gene Therapy for CNS Summit is set to unite key leaders across the gene therapy space, focused on targeting the CNS to treat important neurodegenerative disorders. You can expect to meet C-Level Leaders, Directors, Vice Presidents, Heads, and Scientists all within discovery, research, translational development, clinical development, and regulatory affairs.

This is a must-attend meeting to ensure you are networking with like-minded colleagues facing the same daily challenges surrounding vector development, BBB crossing, identifying accurate CNS models and more – to jointly overcome them and move the needle forward on gene therapy development.

Hanson Wade creates a very immersive environment at these summits which, along with a high quality of speakers, makes for very comfortable and productive networking

Sue Brown, Chief Scientific Officer, Passage Bio

Key Focus Areas of This Year’s Agenda:

Optimizing Capsid Delivery

Find the right capsid to successfully deliver your gene therapy to the brain and reduce off-target toxicities with Novartis

Advancing BBB Penetration

Analyze novel engineered AAV capsids that bind to BBB receptors to improve clinical translation with Affinia Therapeutics

Enhancing Design with AI

Understand the nuances of machine-guided design of AAV capsids to improve pan-brain efficacy with Dyno Therapeutics

Expanding Patient Reach

Target the giants of neurodegenerative diseases and widen your patient pool with Sanofi

Scaling Vector Technologies

Understand the hurdles in scaling up vector technologies to prevent upstream manufacturing setbacks with Ultragenyx

Download the Brochure to Explore Sessions Covering the Focus Areas Outlined Above

  • 70% New Speaker Faculty – Hear fresh perspectives and insights from industry-leading experts.
  • 5+ Hours of Networking – Connect with like-minded peers from across the gene therapy and CNS communities.
  • 2 Pre-Conference Workshops
    • Delivery Devices – Gain a deeper understanding of systemic delivery vs. CSF and brain injections to better target hard-to-treat indications.
    • Regulatory Updates – Navigate evolving guidance and streamline IND submissions to accelerate your path to clinical trials.
7th Gene Therapy for CNS Summit 2025 Brochure Thumbnail

Stay Ahead of the Curve in CNS Gene Therapy Innovation

With recent groundbreaking advancements shaking up the CNS gene therapy space, now is the time to join leading experts shaping the future of targeted delivery.

  • FDA Approves First Brain-Delivered AAV Gene Therapy
    In a historic first, the FDA has approved an AAV gene therapy directly delivered to the brain, marking a major milestone for neuro-focused treatments.
  • Capsida Secures IND Clearance for IV-Delivered CNS Gene Therapy
    Capsida has received FDA IND clearance for its first-in-class intravenously administered gene therapy for STXBP1-related epileptic encephalopathy, underscoring the growing focus on targeted, non-invasive delivery approaches.
  • Dyno Therapeutics Launches Breakthrough Capsids for CNS, Eye & Muscle
    Dyno Therapeutics has unveiled three next-gen capsid delivery vectors, promising to enhance precision and efficiency for CNS-targeted therapies.
    ⭐ Don’t miss insights from Eric Kelsic, CEO & Co-founder of Dyno, speaking live at the meeting. Read more ›
  • Sangamo and Lilly Sign CNS Capsid Licensing Deal
    In another signal of accelerating progress, Sangamo Therapeutics has entered a licensing agreement with Eli Lilly to advance novel CNS-targeted capsids.
    ⭐ Gain first-hand insights from Mohammad Samie, Associate Director, Program Leadership at Sangamo, who will be speaking at the event. Read more ›

Who Will You Meet?

Gene Therapy CNS Summit - Seniority Breakdown
Gene Therapy CNS Summit - Company Type

Have more specific questions about attending companies or their sessions?

Download the full brochure here or email us directly at info@hansonwade.com — we’re happy to help!